Research

Bone and Calcium

Below are some of the current active paediatric studies related to metabolic bone disease in children and adolescents in the U.K. Details can be found on clinicaltrials.gov

  • NCT02163577: Study of KRN23, a Recombinant Fully Human Monoclonal Antibody Against FGF23, in Pediatric Subjects With X-linked Hypophosphatemia (XLH)
  • NCT02915705: Efficacy and Safety of KRN23 Versus Oral Phosphate and Active Vitamin D Treatment in Pediatric Patients With X Linked Hypophosphatemia (XLH) (PIXLES)
  • NCT02306720: An Observational, Longitudinal, Prospective, Long-Term Registry Of Patients With Hypophosphatasia (HPP)
  • NCT03193476: Registry for Patients With X-linked Hypophosphatemia (XLHRegistry)
  • NCT02352753: Multicenter, Single-arm Study to Evaluate Efficacy, Safety, & Pharmacokinetics of Denosumab in Children w/ OI (OI)
  • NCT02724228: A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)